Niemann-Pick Disease, Type A
Synonyms
Cholesterol Lipidoses, Neuronal
Cholesterol Lipidoses, Sphingomyelin
Cholesterol Lipidosis, Neuronal
Cholesterol Lipidosis, Sphingomyelin
Classical Niemann Pick Disease
Classical Niemann-Pick Disease
Deficiencies, Sphingomyelinase
Deficiency, Sphingomyelinase
Lipidoses, Neuronal Cholesterol
Lipidoses, Sphingomyelin
Lipidoses, Sphingomyelin Cholesterol
Lipidosis, Neuronal Cholesterol
Lipidosis, Sphingomyelin
Lipidosis, Sphingomyelin Cholesterol
Neuronal Cholesterol Lipidoses
Neuronal Cholesterol Lipidosis
Niemann Pick Disease, Acute Neuronopathic Form
Niemann Pick Disease, Acute Neurovisceral Form
Niemann Pick Disease, Neuronopathic Type
Niemann Pick Disease, Type A
Niemann Pick's Disease Type A
Niemann-Pick Disease, Acute Neuronopathic Form
Niemann-Pick Disease, Acute Neurovisceral Form
Niemann-Pick Disease, Classical
Niemann-Pick Disease, Neuronopathic Type
Niemann-Pick's Disease Type A
Ophthalmoplegia, Supraoptic Vertical
Ophthalmoplegias, Supraoptic Vertical
Sphingomyelin Cholesterol Lipidoses
Sphingomyelin Cholesterol Lipidosis
Sphingomyelin Lipidoses
Sphingomyelin Lipidosis
Sphingomyelinase Deficiencies
Sphingomyelinase Deficiency
Sphingomyelinase Deficiency Disease
Sphingomyelinase Deficiency Diseases
Supraoptic Vertical Ophthalmoplegia
Supraoptic Vertical Ophthalmoplegias
Type A Niemann Pick Disease
Type A Niemann-Pick Disease
Vertical Ophthalmoplegia, Supraoptic
Vertical Ophthalmoplegias, Supraoptic
The classic infantile form of Niemann-Pick Disease, caused by mutation in SPHINGOMYELIN PHOSPHODIESTERASE. It is characterized by accumulation of SPHINGOMYELINS in the cells of the MONONUCLEAR PHAGOCYTE SYSTEM and other cell throughout the body leading to cell death. Clinical signs include JAUNDICE, hepatosplenomegaly, and severe brain damage.